(PRWEB UK) 1 October 2012
As recently reported in Nature, UniQure have won recommendation to market the western world’s first gene therapy, Glybera. The company’s success is a huge step towards a long-cherished goal of gene therapy: delivering, in a single treatment, a life-long, functional copy of a missing gene to patients.
Jörn Aldag, chief executive of UniQure, says that the announcement from the EMA is an “overdue signal” to the gene-therapy community that things are changing. “It unlocks the potential,” he says, quoted in Nature. “You will see more investment coming.”*
Perhaps as important is UniQure’s pioneering “annuity” approach to reimbursement, staggering payments over the five years for which treatment has been proved to work. As highlighted by the Financial Times, such financial innovation may prove as important as the scientific breakthroughs that led to the treatment in the first place**.
Other keynote speakers presenting at this outstanding event include:
Visit http://www.smi-online.co.uk/goto/orphandrugs-event38.asp to secure your place now!
Alternatively, contact Alternatively Contact Fateja Begum on telephone +44 (0) 20 7827 6184 or email on firstname.lastname@example.org
About SMi Group
The SMi Group is a world leader in business to business information. With nearly two decades in the business, thousands of senior executives from blue chip companies have already benefitted from SMi’s highly targeted conferences, workshops and publications. For more information visit: